Casey is treating patients with Luxturna--the first gene therapy treatment for inherited disease caused by a single gene to come on the U.S. market. Gene therapy is a potentially transformative treatment which will have lifelong effects for children at risk of going blind from inherited retinal eye disorder. This new medical advance will have a major impact on their quality of life. 

Learn more about 4-year old Caspian, one of the first to benefit from this groundbreaking treatment.