Markus Grompe, M.D.
"Evaluation of resveratrol and N-acetylcysteine for cancer chemoprevention in a Fanconi anemia murine model,"
"Fumarylacetoacetate hydrolase deficient pigs are a novel large animal model of metabolic liver disease,"
"Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype,"
"Pharmacologic inhibition of L-tyrosine degradation ameliorates cerebral dopamine deficiency in murine phenylketonuria (PKU),"
"Selection and evaluation of clinically relevant AAV variants in a xenograft liver model,"